One-Shot Gene Therapy Cure $665K

GlaxoSmithKline is offering a one-shot cure, called Strimveli, for a bone marrow disease called ADA-SCID, a sometimes fatal inability to fight infections. The cost: $665,000, making it the most expensive one-time treatment sold by any drug firm. (But it comes with a guarantee.)

The idea behind gene therapy is that a one-time correction to a patient’s DNA will lead to a lifelong cure. Strimvelis is the first treatment to be commercialized that lives up to the promise. But potential cures for hemophilia, a rare eye disease, and a fatal brain illness could reach the market next, and they could be similarly expensive.

“We do not expect to recover all of the costs of building a platform to deliver gene and cell therapy from Strimvelis alone,” says Anna Padula, a spokesperson for GSK’s rare-diseases group. “We hope that Strimvelis will be the first of a number of innovative gene-therapy medicines that we will bring to patients.” The company recognizes, she adds, “that the industry will need to adapt the way in which medicines are priced and funded.”

In reading about this, I was reminded of the cure offered to Case, the protagonist of William Gibson's 1984 novel Neuromancer. It's not a very close match, but the idea of a single treatment offering a complete cure is striking. Case had been given a mycotoxin that burned out subtle areas of his nervous system and his ability to jack into cyberspace was lost.

"What would you say if I told you we could correct the damage, Case?" Ermitage suddenly looked to Case as if he were carved from a block of metal; inert, enormously heavy...

"It'll work, Case. You got no idea, the kind of stuff Armitage has. Like he's gonna pay these nerve boys for fixing you with th program he's giving them to tell them how to do it...

Cold steel odor. Ice caressed his spine.

Then black fire found the branching tributaries of the nerves...

He woke... "My back hurts."

That's where they replaced your fluid... some new stuff patched into your liver. The nerve stuff, I dunno. Lot of injections. They didn't have to open anything up for the main show..."

Read about other gene therapies at Gene Therapy Could Restore Hearing To The Deaf and Gene Therapy Builds Muscles Fast. Via Technology Review.

Scroll down for more stories in the same category. (Story submitted 8/4/2016)

Follow this kind of news @Technovelgy.

| Email | RSS | Blog It | Stumble | del.icio.us | Digg | Reddit |

Would you like to contribute a story tip? It's easy:
Get the URL of the story, and the related sf author, and add it here.

Comment/Join discussion ( 0 )

Related News Stories - (" Medical ")

3D Printed Bionic Chinese Skin
Designer skin for everyone!

Drug Creates Real Melanin Tan
I've used them all my life...

Medical Drones Hover Like Angels Near You
'The death-reversal equipment is on its way...'- Frederk Pohl, 1965.

Vaccine Blocks Heroin High
'You're biochemically incapable of getting off...' - William Gibson, 1985.

 

Google
  Web TechNovelgy.com   

Technovelgy (that's tech-novel-gee!) is devoted to the creative science inventions and ideas of sf authors. Look for the Invention Category that interests you, the Glossary, the Invention Timeline, or see what's New.

 

 

 

 

 

Current News

MULTI Model Of Star Trek Turbolift
Cool prototype video!

A Look Into The Future Of Spacecraft!
Ever wonder how you look when you enter a new part of a spacecraft?

An 'Ethical Black Box' For Robots?
Explored by science fiction authors.

Dadbot Digital Immortality
'A hardwired ROM cassette replicating a dead man's skills...'

Should We Permit Computers To Create Their Own Language?
'Talk Between Robots radio...'

Breakthrough Starshot Sprites Yearn For Alpha Centauri
'Whoever launched it fired a laser cannon...'

Kino Project Roaming Personal Fashion Robots
'Most of the crew have the tiny imp ride on their shoulder...'

Astronaut Exercise Video, Predicted By SF Writers
'Joe got out the gravity-simulator harnesses.'

First Crewless Ship? Umm
Autonomous Spaceport Drone Ship?

RFID Chipped Employees Of Three Square Market
'About a third of the people in Manhattan have replaced their Freedom Card with a radio-frequency chip...'

JAXA's Int-Ball Drone To Follow Astronauts In Space Station
'I want you to build me some of those.'

Amazon Patents Annoying Robot That Follows You
'The... machine, being homotropic, headed toward them, still bleating...'

Hand Gestures And Body Poses Control Devices
'He waved his hand... the circuit switched...'

Rovable Robots Crawl Across Your Body
'Most of the crew have the tiny imp ride on their shoulder...'

Sansar Social Virtual Reality Platform In 2017?
'And just as a daydreamer forgets his actual surroundings, and sees other realities...'

Cellphone Harvests Power From Ambient Radio Signals And Light
A battery-free phone.

More SF in the News Stories

More Beyond Technovelgy science news stories

Home | Glossary | Invention Timeline | Category | New | Contact Us | FAQ | Advertise |
Technovelgy.com - where science meets fiction™

Copyright© Technovelgy LLC; all rights reserved.